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PepGen developed a POC drug, PGN-EDO51, using its enhanced delivery oligonucleotide platform, which skips exon 51 in the DMD gene

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Silencing RNA (siRNA) knockdown of Muc5b was shown to decrease IL-1 levels but did not alter IL-1 levels in a CFTR knockout rat model infected with P

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doi: 10.1146/annurev-biochem-063011-092449 44 LagenaurLASanders-BeerBEBrichacekBPalRLiuXLiuYet al

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